this post was submitted on 18 Jan 2024
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[–] solrize@lemmy.world 18 points 9 months ago

Exa-cel, also known by its brand name Casgevy, received its first regulatory approval on Nov. 16, 2023 from the U.K. Medicines and Healthcare products Regulatory Agency (MHRA) to treat two debilitating blood disorders: sickle-cell disease and transfusion-dependent beta-thalassemia. The U.S. Food and Drug Administration (FDA) later approved the therapy as a treatment for both disorders.